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Pag-aaral pangklinika para sa Mga Neuromuscular Disorders sa California
6 pag-aaral para sa Mga Neuromuscular Disorders ang naghahanap ng mga kalahok sa mga site sa California.
Opisyal na teksto ng pag-aaral (English)
A Study to Investigate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AZD5492 in Adult Participants With Systemic Lupus Erythematosus or Idiopathic Inflammatory Myopathies or Rheumatoid Arthritis.
- Research Site, La Jolla
- Research Site, Sacramento
Nagre-recruitPhase 1
Edad 18 hanggang 70 · Lahat ng kasarian · Na-update Set 15, 2026 · NCT06916806A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
- University of California, Irvine (UCI), Irvine
- Stanford Neuroscience Health Center, Palo Alto
Nagre-recruitPhase 1/2
Edad 18 hanggang 65 · Lahat ng kasarian · Na-update Hul 20, 2026 · NCT07282847Connect-One: Early Feasibility Study of Connexus® Brain-Computer Interface (BCI)
- University of California, Davis, Sacramento
Nagre-recruit
Edad 22 hanggang 75 · Lahat ng kasarian · Na-update Abr 14, 2026 · NCT07357428Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Stanford University, Palo Alto
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 5 pataas · Lahat ng kasarian · Na-update Abr 9, 2026 · NCT06839469Mesenchymal Stem Cells for the Treatment of Various Chronic and Acute Conditions
- Southern California Hospital at Culver City / Southern California Hospital at Hollywood / Multiple US-based Sub-Investigator Sites, Culver City
Nagre-recruitPhase 1/2Malugod na tinatanggap ang malusog na boluntaryo
Edad 18 pataas · Lahat ng kasarian · Na-update Abr 29, 2022 · NCT04684602Congenital Muscle Disease Study of Patient and Family Reported Medical Information
- Congenital Muscle Disease International Registry (www.cmdir.org), Lakewood
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Ago 9, 2021 · NCT01403402Mula sa ClinicalTrials.gov, na-kuha noong Okt 1, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.