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Pag-aaral pangklinika para sa Phenylketonuria na nagre-recruit sa U.S.

14 pag-aaral para sa Phenylketonuria ang nagre-recruit ng mga kalahok sa mga site sa buong Estados Unidos.

Mga lungsod na may pinakamaraming pag-aaral

Ayos sa estado

Mga pag-aaral na kamakailan lamang in-update

Opisyal na teksto ng pag-aaral (English)

A Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AG-181 in Subjects With Phenylketonuria

Nagre-recruitPhase 1
Edad 18 hanggang 69 · Lahat ng kasarian · Na-update Set 28, 2026 · NCT07241234

A Study of Sepiapterin in Participants With Phenylketonuria (PKU)

Nagre-recruitPhase 3
Hanggang edad 9 · Lahat ng kasarian · Na-update Ago 28, 2026 · NCT06302348

PheCheck™ Validation Study

Nagre-recruitObservasyonal na pag-aaral
Edad 1 pataas · Lahat ng kasarian · Na-update Ago 25, 2026 · NCT07551921

A Study of MZE782 in Adults With PKU

Nagre-recruitPhase 2
Edad 18 hanggang 75 · Lahat ng kasarian · Na-update Ago 20, 2026 · NCT07694440

AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)

Nagre-recruitPhase 1/2
Edad 18 hanggang 55 · Lahat ng kasarian · Na-update Ago 18, 2026 · NCT06332807

A Trial to Examine if Repinatrabit is Processed Differently in Adults With Reduced Liver or Kidney Function Compared to Adults With Normal Liver and Kidney Function

Nagre-recruitPhase 1Malugod na tinatanggap ang malusog na boluntaryo
Edad 18 hanggang 65 · Lahat ng kasarian · Na-update Ago 12, 2026 · NCT07713758

A Study of JNT-517 in Participants With Phenylketonuria (PKU)

Nagre-recruitPhase 3
Edad 18 pataas · Lahat ng kasarian · Na-update Hul 8, 2026 · NCT06971731

Immune Modulation During Palynziq® Treatment in Adults (IMPALA)

Nagre-recruitPhase 4
Edad 18 hanggang 65 · Lahat ng kasarian · Na-update Hun 17, 2026 · NCT07477691

Educational, Social Support, and Nutritional Interventions and Their Cumulative Effect on Pregnancy Outcomes and Quality of Life in Teen and Adult Women With Phenylketonuria

Nagre-recruitMalugod na tinatanggap ang malusog na boluntaryo
Edad 11 pataas · Kababaihan · Na-update May 7, 2026 · NCT01659749

A Long-Term Study of JNT-517 in Participants With Phenylketonuria

Nagre-recruitPhase 3
Edad 4 pataas · Lahat ng kasarian · Na-update May 1, 2026 · NCT06628128

A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)

Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Mar 25, 2026 · NCT05813678

A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)

Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Mar 24, 2026 · NCT06305234

Nutritional Impacts of Palynziq on Patients With Phenylketonuria (PKU)

Nagre-recruitObservasyonal na pag-aaral
Edad 16 pataas · Lahat ng kasarian · Na-update Ene 14, 2026 · NCT04404530

Development of Novel Psychological Assessment Tools and Anxiety Intervention for Phenylketonuria

Nagre-recruit
Edad 10 hanggang 17 · Lahat ng kasarian · Na-update Dis 23, 2025 · NCT06560736

Mula sa ClinicalTrials.gov, na-kuha noong Set 30, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.