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Pag-aaral pangklinika para sa Rare Diseases sa North Carolina

6 pag-aaral para sa Rare Diseases ang naghahanap ng mga kalahok sa mga site sa North Carolina.

Mga Lungsod sa North Carolina

Opisyal na teksto ng pag-aaral (English)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • Duke University Health System, Durham
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
1 Month – 100 Years · Lahat ng kasarian · Na-update Okt 2, 2026 · NCT02450851

Odevixibat Pregnancy and Lactation Surveillance Program: A Study to Evaluate the Safety of Odevixibat During Pregnancy and/or Lactation

  • Virtual Research Coordination Center Odevixibat (BYLVAY) Pregnancy Surveillance Program, Wilmington
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Kababaihan · Na-update Okt 1, 2026 · NCT06258902

Elafibranor Pregnancy Surveillance Program: A Study to Evaluate the Safety of Elafibranor During Pregnancy

  • Virtual Research Coordination Center, Wilmington
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Kababaihan · Na-update Ago 31, 2026 · NCT07556913

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

  • Duke University / Lenox Baker Children's Hospital, Durham
Nagre-recruitObservasyonal na pag-aaral
Edad 6 pataas · Lahat ng kasarian · Na-update Hul 2, 2026 · NCT07127978

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Duke University Medical Center, Durham
Nagre-recruitPhase 2
Edad 18 pataas · Lahat ng kasarian · Na-update Hun 23, 2026 · NCT07123155

The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis

  • Wake Forest University Health Sciences, Winston-Salem
Nagre-recruitPhase 2
Edad 12 pataas · Lahat ng kasarian · Na-update Hul 1, 2025 · NCT04372615

Mula sa ClinicalTrials.gov, na-kuha noong Okt 6, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.