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Pag-aaral pangklinika para sa Rett Syndrome sa California
4 pag-aaral para sa Rett Syndrome ang naghahanap ng mga kalahok sa mga site sa California.
Mga Lungsod sa California
Opisyal na teksto ng pag-aaral (English)
Rett Syndrome Registry
- Children's Hospital Los Angeles, Los Angeles
- UCSF Benioff Children's Hospital, Oakland
- Rady Children's Hospital - San Diego, San Diego
Nagre-recruitObservasyonal na pag-aaral
Edad 0 hanggang 99 · Lahat ng kasarian · Na-update Hun 30, 2026 · NCT05432349To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome
- Biomed Testing Facility # BIO-05-92093, La Jolla
- Biomed Testing Facility # BIO-04-90095, Los Angeles
- Biomed Testing Facility # BIO-03-95817, Sacramento
- at 1 pa
Nagre-recruitPhase 3
Edad 5 hanggang 20 · Kababaihan · Na-update Mar 27, 2026 · NCT06840496ATTUNE: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION440 in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome (MDS)
- Rady Children's Hospital, San Diego
Nagre-recruitPhase 1/2
Edad 2 hanggang 65 · Kalalakihan · Na-update Mar 24, 2026 · NCT06430385Neurophysiologic Biomarkers in Rett Syndrome
- Children's Hospital of Los Angeles, Los Angeles
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 1 hanggang 18 · Kababaihan · Na-update Okt 20, 2025 · NCT05932589Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.