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Pag-aaral pangklinika para sa Transthyretin-Related Hereditary Amyloidosis sa California

5 pag-aaral para sa Transthyretin-Related Hereditary Amyloidosis ang naghahanap ng mga kalahok sa mga site sa California.

Mga Lungsod sa California

Opisyal na teksto ng pag-aaral (English)

Non-interventional Study of Patients With Transthyretin (ATTR) Amyloidosis

  • Research Site, La Jolla
  • Research Site, Los Angeles
  • Research Site, San Francisco
  • at 1 pa
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 130 · Lahat ng kasarian · Na-update Set 23, 2026 · NCT06465810

Long-term Safety of Eplontersen Treated aTTR Patients and in Liver Transplant and Severely Hepatic Impaired Subpopulations

  • Research Site, Los Angeles
Nagre-recruitObservasyonal na pag-aaral
Edad 18 pataas · Lahat ng kasarian · Na-update Set 14, 2026 · NCT07654855

ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)

  • Clinical Trial Site, La Jolla
  • Clinical Trial Site, Los Angeles
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Set 8, 2026 · NCT04561518

Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant

  • University of California, San Diego (UCSD) - Medical Center, La Jolla
  • University of California, Los Angeles (UCLA) - David Geffen School of Medicine, Los Angeles
  • University of California, San Francisco (UCSF), San Francisco
  • at 1 pa
Nagre-recruitPhase 3
Edad 18 hanggang 75 · Lahat ng kasarian · Na-update Ago 4, 2026 · NCT06563895

MAGNITUDE: A Phase 3 Study of NTLA-2001 in Participants With Transthyretin Amyloidosis With Cardiomyopathy (ATTR-CM)

  • Cedars-Sinai Medical Center, Los Angeles
  • Western Greater Los Angeles VA Medical Center, Los Angeles
  • Stanford University, Palo Alto
  • at 1 pa
Nagre-recruitPhase 3
Edad 18 hanggang 90 · Lahat ng kasarian · Na-update Mar 27, 2026 · NCT06128629

Mula sa ClinicalTrials.gov, na-kuha noong Okt 6, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.