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Sgrùdaidhean clionaigeach Adrenoleukodystrophy ann an Pennsylvania

Tha 4 sgrùdaidhean airson Adrenoleukodystrophy a’ lorg phàirtichean aig làraichean ann an Pennsylvania.

Bailtean ann an Pennsylvania

Teacsa sgrùdaidh oifigeil (Beurla)

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
A’ fastadhSgrùdadh amharc
2 Months – 60 Years · Gach gnè · Air ùrachadh 13 Faoi 2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
A’ fastadhÌre 2
2 Months – 55 Years · Gach gnè · Air ùrachadh 15 Dùbh 2025 · NCT01962415

The Myelin Disorders Biorepository Project

  • The Children's Hospital of Philadelphia, Philadelphia
  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh Medical Center, Pittsburgh
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 23 Dàmh 2025 · NCT03047369

A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcel

  • Children's Hospital of Philadelphia, Philadelphia
A’ fastadhSgrùdadh amharc
Gach aois · Fir · Air ùrachadh 2 Iuch 2025 · NCT06224413

Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.