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Sgrùdaidhean clionaigeach Alpha-Mannosidosis a’ fastadh anns na SA

Tha 5 sgrùdaidhean airson Alpha-Mannosidosis a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.

Bailtean leis na sgrùdaidhean as motha

Le stàit

Sgrùdaidhean air an ùrachadh o chionn ghoirid

Teacsa sgrùdaidh oifigeil (Beurla)

UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

A’ fastadhÌre 1
1 Week – 22 Years · Gach gnè · Air ùrachadh 3 Sult 2026 · NCT02254863

Longitudinal Study of Neurodegenerative Disorders

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 9 Gearr 2026 · NCT03333200

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

A’ fastadhSgrùdadh amharc
2 Months – 60 Years · Gach gnè · Air ùrachadh 13 Faoi 2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

A’ fastadhÌre 2
2 Months – 55 Years · Gach gnè · Air ùrachadh 15 Dùbh 2025 · NCT01962415

Analysis of Velmanase Alfa (Lamzede®)'s Effects in the Body of Children With Alpha-Mannosidosis Under the Age 3

A’ fastadhSgrùdadh amharc
Suas gu aois 3 · Gach gnè · Air ùrachadh 16 Cèit 2025 · NCT06184503

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.