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Sgrùdaidhean clionaigeach Galar Fabry a’ fastadh anns na SA

Tha 10 sgrùdaidhean airson Galar Fabry a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.

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Teacsa sgrùdaidh oifigeil (Beurla)

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

A’ fastadhÌre 1/2
Aoisean 18 gu 65 · Fir · Air ùrachadh 24 Sult 2026 · NCT06270316

A Study of Patients With Fabry Disease (US Specific)

A’ fastadhSgrùdadh amharc
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 9 Sult 2026 · NCT06906367

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

A’ fastadhÌre 3
Aoisean 2 gu 11 · Gach gnè · Air ùrachadh 1 Sult 2026 · NCT06904261

Natural History and Structural Functional Relationships in Fabry Renal Disease Treatment Outcomes(Changes)in Fabry Renal Disease Study

A’ fastadhSgrùdadh amharc
Aoisean 1 gu 75 · Gach gnè · Air ùrachadh 14 Lùna 2026 · NCT01581424

Cardiovascular Multimodality Imaging Study

A’ fastadhSgrùdadh amharc
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 10 Lùna 2026 · NCT06610019

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease

A’ fastadhÌre 2/3
Aoisean 2 gu 17 · Gach gnè · Air ùrachadh 10 Lùna 2026 · NCT06328608

Fabry Disease Registry & Pregnancy Sub-registry

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 23 Ògmh 2026 · NCT00196742

A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients

A’ fastadhSgrùdadh amharc
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 14 Samh 2025 · NCT06663358

A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding

A’ fastadhSgrùdadh amharc
Gach aois · Banairean · Air ùrachadh 8 Iuch 2025 · NCT04252066

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.