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Sgrùdaidhean clionaigeach Galairean Ginteil ann an North Carolina

Tha 9 sgrùdaidhean airson Galairean Ginteil a’ lorg phàirtichean aig làraichean ann an North Carolina.

Bailtean ann an North Carolina

Teacsa sgrùdaidh oifigeil (Beurla)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • Duke University Health System, Durham
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
1 Month – 100 Years · Gach gnè · Air ùrachadh 2 Dàmh 2026 · NCT02450851

Inherited Reproductive Disorders

  • NIEHS Clinical Research Unit (CRU), Research Triangle Park
A’ fastadhSgrùdadh amharc
6 Weeks – 120 Years · Gach gnè · Air ùrachadh 28 Iuch 2026 · NCT01500447

Rett Syndrome Registry

  • The University of North Carolina at Chapel Hill, Chapel Hill
A’ fastadhSgrùdadh amharc
Aoisean 0 gu 99 · Gach gnè · Air ùrachadh 30 Ògmh 2026 · NCT05432349

Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)

  • Rare Disease Research, LLC, Hillsborough
A’ fastadhÌre 3
Aoisean 4 gu 18 · Fir · Air ùrachadh 27 Cèit 2026 · NCT07608432

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

  • Levine Children's Hospital - Hematology, Charlotte
A’ fastadhÌre 3
Aoisean 12 gu 35 · Gach gnè · Air ùrachadh 23 Màrt 2026 · NCT05477563

Helix Research Network

  • Cone Health (Gene Connect), Burlington
  • WakeMed (PreciselyYou), Raleigh
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 23 Màrt 2026 · NCT06057181

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • Duke University Medical System (Duke Health), Durham
A’ fastadhÌre 1/2
Aoisean 1 agus nas sine · Gach gnè · Air ùrachadh 23 Màrt 2026 · NCT05130437

PKP2-ACM Natural History Study

  • Duke University, Durham
A’ fastadhSgrùdadh amharc
Aoisean 12 agus nas sine · Gach gnè · Air ùrachadh 27 Gearr 2026 · NCT06644742

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Duke University Medical System (Duke Health), Durham
A’ fastadhÌre 1/2
Gach aois · Gach gnè · Air ùrachadh 22 Faoi 2026 · NCT04159103

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.