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Sgrùdaidhean clionaigeach Galar Stòraidh Glycogen Seòrsa II ann an California

Tha 5 sgrùdaidhean airson Galar Stòraidh Glycogen Seòrsa II a’ lorg phàirtichean aig làraichean ann an California.

Bailtean ann an California

Teacsa sgrùdaidh oifigeil (Beurla)

A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease

  • University of California-Irvine, Irvine
A’ fastadhÌre 1
Aoisean 18 gu 75 · Gach gnè · Air ùrachadh 17 Lùna 2026 · NCT07354724

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

  • University of California, Irvine (UCI), Irvine
  • Stanford Neuroscience Health Center, Palo Alto
A’ fastadhÌre 1/2
Aoisean 18 gu 65 · Gach gnè · Air ùrachadh 20 Iuch 2026 · NCT07282847

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • University of California - Irvine Medical Center, Irvine
A’ fastadhÌre 2
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 23 Ògmh 2026 · NCT07123155

Pompe Disease Registry Protocol

  • University of California at Irvine- Site Number : 840036, Irvine
  • Southern California Permanente Medical Group- Site Number : 840108, Los Angeles
  • Children's Hospital of Orange County- Site Number : 840074, Orange
  • agus 3 a bharrachd
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 23 Ògmh 2026 · NCT00231400

A Global Prospective Observational Registry of Patients With Pompe Disease

  • University of California Irvine, Irvine
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 10 Màrt 2026 · NCT06121011

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.