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Sgrùdaidhean clionaigeach Galar Stòraidh Glycogen Seòrsa II ann an New York

Tha 4 sgrùdaidhean airson Galar Stòraidh Glycogen Seòrsa II a’ lorg phàirtichean aig làraichean ann an New York.

Bailtean ann an New York

Teacsa sgrùdaidh oifigeil (Beurla)

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

  • NYU Langone, New York
A’ fastadhÌre 1/2
Aoisean 18 gu 65 · Gach gnè · Air ùrachadh 20 Iuch 2026 · NCT07282847

Pompe Disease Registry Protocol

  • NYU Langone Health - Perlmutter Cancer Center - Huntington- Site Number : 840040, Huntington
  • Northwell Health- Site Number : 840102, New Hyde Park
  • Icahn School of Medicine at Mount Sinai- Site Number : 840005, New York
  • agus 4 a bharrachd
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 23 Ògmh 2026 · NCT00231400

Pompe Pregnancy Sub-Registry

  • New York University School Of Medicine- Site Number : 840040, New York
  • Mt. Sinai School of Medicine- Site Number : 840005, New York
  • Columbia University Irving Medical Center- Site Number : 157199, New York
A’ fastadhSgrùdadh amharc
Gach aois · Banairean · Air ùrachadh 16 Gibl 2026 · NCT00567073

A Global Prospective Observational Registry of Patients With Pompe Disease

  • NYU Neurogenetics, NYU Langone Medical Center, New York
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 10 Màrt 2026 · NCT06121011

Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.