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Sgrùdaidhean clionaigeach Galar Stòraidh Glycogen Seòrsa II ann an Virginia

Tha 6 sgrùdaidhean airson Galar Stòraidh Glycogen Seòrsa II a’ lorg phàirtichean aig làraichean ann an Virginia.

Bailtean ann an Virginia

Teacsa sgrùdaidh oifigeil (Beurla)

A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease

  • The Lysosomal & Rare Disorders Research & Treatment Center, Fairfax
A’ fastadhÌre 1
Aoisean 18 gu 75 · Gach gnè · Air ùrachadh 17 Lùna 2026 · NCT07354724

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

  • Virginia Commonwealth University (VCU), Richmond
A’ fastadhÌre 1/2
Aoisean 18 gu 65 · Gach gnè · Air ùrachadh 20 Iuch 2026 · NCT07282847

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Lysosomal and Rare Disorders Research and Treatment Center (LDRTC), Fairfax
A’ fastadhÌre 2
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 23 Ògmh 2026 · NCT07123155

Pompe Disease Registry Protocol

  • O & O Alpan- Site Number : 840025, Fairfax
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 23 Ògmh 2026 · NCT00231400

Pompe Pregnancy Sub-Registry

  • O & O Alpan- Site Number : 840025, Fairfax
A’ fastadhSgrùdadh amharc
Gach aois · Banairean · Air ùrachadh 16 Gibl 2026 · NCT00567073

A Global Prospective Observational Registry of Patients With Pompe Disease

  • Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 10 Màrt 2026 · NCT06121011

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.