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Sgrùdaidhean clionaigeach Hemophilia B ann an California

Tha 7 sgrùdaidhean airson Hemophilia B a’ lorg phàirtichean aig làraichean ann an California.

Bailtean ann an California

Teacsa sgrùdaidh oifigeil (Beurla)

Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively

  • The Regents of the University of California||UC Davis Health, Rancho Cordova
  • UC Davis Health, Sacramento
  • UC Davis Ambulatory Care Clinic, Sacramento
  • agus 3 a bharrachd
A’ fastadhÌre 3
Aoisean 18 agus nas sine · Fir · Air ùrachadh 2 Dàmh 2026 · NCT05568719

Phase 3, Open-label, Single-dose Study of CSL222 in Adolescent Male Subjects (≥ 12 to < 18 Years of Age) With Severe or Moderately Severe Hemophilia B

  • Center for Inherited Blood Disorders, Orange
A’ fastadhÌre 3
138 Months – 206 Months · Fir · Air ùrachadh 16 Sult 2026 · NCT07080905

A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B

  • Orthopaedic Hemophilia Treatment Center, Los Angeles
  • David Geffen School of Medicine at UCLA, Los Angeles
  • Children's Hospital Los Angeles, Los Angeles
  • agus 2 a bharrachd
A’ fastadhÌre 1/2
Aoisean 2 agus nas sine · Fir · Air ùrachadh 11 Sult 2026 · NCT06379789

Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs)

  • University of California, San Diego (UCSD), San Diego
A’ fastadhÌre 3
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 27 Lùna 2026 · NCT06003387

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Orthopaedic Institute for Children HTC, Los Angeles
  • Childrens Hospital Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital Oakland, Oakland
  • agus 5 a bharrachd
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 17 Lùna 2026 · NCT04398628

A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)

  • Children's Hospital Los Angeles, Los Angeles
A’ fastadhÌre 1Fàilte do shaor-thoilich fhallain
Aoisean 18 gu 60 · Gach gnè · Air ùrachadh 2 Iuch 2026 · NCT06349473

SEVENFACT® for Bleeding Events in Hemophilia With Inhibitors

  • Orthopaedic Institute for Children, Los Angeles
  • University of California at Davis UC Davis Hemostasis and Thrombosis Center, Sacramento
A’ fastadhÌre 4
Aoisean 12 gu 100 · Gach gnè · Air ùrachadh 12 Faoi 2026 · NCT04647227

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.