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Sgrùdaidhean clionaigeach Leukodystrophies a’ fastadh anns na SA

Tha 8 sgrùdaidhean airson Leukodystrophies a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.

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Sgrùdaidhean air an ùrachadh o chionn ghoirid

Teacsa sgrùdaidh oifigeil (Beurla)

UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

A’ fastadhÌre 1
1 Week – 22 Years · Gach gnè · Air ùrachadh 3 Sult 2026 · NCT02254863

Krabbe Disease Global Patient Registry

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 17 Iuch 2026 · NCT02993796

A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)

A’ fastadhÌre 1/2
30 Months · Gach gnè · Air ùrachadh 17 Gibl 2026 · NCT04998396

Longitudinal Study of Neurodegenerative Disorders

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 9 Gearr 2026 · NCT03333200

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

A’ fastadhSgrùdadh amharc
2 Months – 60 Years · Gach gnè · Air ùrachadh 13 Faoi 2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

A’ fastadhÌre 2
2 Months – 55 Years · Gach gnè · Air ùrachadh 15 Dùbh 2025 · NCT01962415

The Myelin Disorders Biorepository Project

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 23 Dàmh 2025 · NCT03047369

Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 29 Cèit 2025 · NCT01793168

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.