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Sgrùdaidhean clionaigeach Leukodystrophies a’ fastadh anns na SA
Tha 8 sgrùdaidhean airson Leukodystrophies a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.
Bailtean leis na sgrùdaidhean as motha
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Sgrùdaidhean air an ùrachadh o chionn ghoirid
Teacsa sgrùdaidh oifigeil (Beurla)
UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
A’ fastadhÌre 1
1 Week – 22 Years · Gach gnè · Air ùrachadh 3 Sult 2026 · NCT02254863Krabbe Disease Global Patient Registry
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 17 Iuch 2026 · NCT02993796A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)
A’ fastadhÌre 1/2
30 Months · Gach gnè · Air ùrachadh 17 Gibl 2026 · NCT04998396Longitudinal Study of Neurodegenerative Disorders
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 9 Gearr 2026 · NCT03333200Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
A’ fastadhSgrùdadh amharc
2 Months – 60 Years · Gach gnè · Air ùrachadh 13 Faoi 2026 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
A’ fastadhÌre 2
2 Months – 55 Years · Gach gnè · Air ùrachadh 15 Dùbh 2025 · NCT01962415The Myelin Disorders Biorepository Project
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 23 Dàmh 2025 · NCT03047369Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 29 Cèit 2025 · NCT01793168Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.