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Sgrùdaidhean clionaigeach Galar metabolach ann an Pennsylvania

Tha 5 sgrùdaidhean airson Galar metabolach a’ lorg phàirtichean aig làraichean ann an Pennsylvania.

Bailtean ann an Pennsylvania

Teacsa sgrùdaidh oifigeil (Beurla)

A Study to Evaluate the Efficacy and Safety of Pegozafermin in Participants With Compensated Cirrhosis Due to MASH

  • 89bio Clinical Study Site, Philadelphia
  • 89bio Clinical Study Site, Pittsburgh
A’ fastadhÌre 3
Aoisean 18 gu 75 · Gach gnè · Air ùrachadh 5 Dàmh 2026 · NCT06419374

Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia

  • Children's Hospital of Pittsburgh, Pittsburgh
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
1 Month – 100 Years · Gach gnè · Air ùrachadh 28 Sult 2026 · NCT02890342

Clinical and Laboratory Study of Methylmalonic Acidemia

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
1 Month – 115 Years · Gach gnè · Air ùrachadh 10 Sult 2026 · NCT00078078

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • The Children's Hospital of Philadelphia (CHOP), Philadelphia
A’ fastadhÌre 1/2
Aoisean 1 agus nas sine · Gach gnè · Air ùrachadh 23 Màrt 2026 · NCT05130437

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Children's Hospital of Philadelphia (CHOP), Philadelphia
A’ fastadhÌre 1/2
Gach aois · Gach gnè · Air ùrachadh 22 Faoi 2026 · NCT04159103

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.