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Dachaigh › Mucopolysaccharidosis IV › California

Sgrùdaidhean clionaigeach Mucopolysaccharidosis IV ann an California

Tha 6 sgrùdaidhean airson Mucopolysaccharidosis IV a’ lorg phàirtichean aig làraichean ann an California.

Teacsa sgrùdaidh oifigeil (Beurla)

Prospective Clinical Assessment Study in Children With Hypochondroplasia

  • UCSF Benioff Children's Hospital, Oakland
A’ fastadhSgrùdadh amharc
30 Months – 16 Years · Gach gnè · Air ùrachadh 16 Iuch 2026 · NCT06410976

Interventional Study of Infigratinib in Children < 3 Years Old With Achondroplasia (ACH)

  • UCSF Benioff Children's Hospital, Oakland
A’ fastadhÌre 2
0 Years – 32 Months · Gach gnè · Air ùrachadh 13 Iuch 2026 · NCT07169279

A Study Evaluating the Impact of Regular FODMAP-targeting Digestive Enzyme Blend Use on Gastrointestinal Symptoms in Individuals With Self-Reported Bloating

  • People Science, Los Angeles
A’ fastadhFàilte do shaor-thoilich fhallain
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 15 Cèit 2026 · NCT07591584

Registry of Patients Diagnosed With Lysosomal Storage Diseases

  • University of California San Francisco, San Francisco
A’ fastadhSgrùdadh amharc
Suas gu aois 64 · Gach gnè · Air ùrachadh 8 Gibl 2026 · NCT05619900

PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

  • University of California, San Francisco
A’ fastadhÌre 1
Aoisean 18 gu 50 · Banairean · Air ùrachadh 17 Màrt 2026 · NCT04532047

Cardiac Structure and Function in MPS

  • Children'S Hospital of Orange County, Orange
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 0 gu 99 · Gach gnè · Air ùrachadh 26 Faoi 2026 · NCT07361536

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.