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Sgrùdaidhean clionaigeach Galar fèithe ann an Pennsylvania

Tha 3 sgrùdaidhean airson Galar fèithe a’ lorg phàirtichean aig làraichean ann an Pennsylvania.

Teacsa sgrùdaidh oifigeil (Beurla)

Efficacy of KL1333 in Adult Patients With Primary Mitochondrial Disease

  • The Children's Hospital of Philadelphia, Philadelphia
  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
A’ fastadhÌre 2
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 26 Ògmh 2026 · NCT05650229

WiTNNess - TNNT1 Myopathy Natural History Study

  • Clinic for Special Children, Gordonville
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 23 Ògmh 2026 · NCT06374719

A Phase 1 Study of Anitocabtagene Autoleucel for the Treatment of Subjects With Non-oncology Plasma Cell-related Diseases

  • Temple University Hospital, Philadelphia
A’ fastadhÌre 1
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 25 Gearr 2026 · NCT06626919

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.