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Sgrùdaidhean clionaigeach Acidemia Propionic a’ fastadh anns na SA

Tha 6 sgrùdaidhean airson Acidemia Propionic a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.

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Sgrùdaidhean air an ùrachadh o chionn ghoirid

Teacsa sgrùdaidh oifigeil (Beurla)

Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia

A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
1 Month – 100 Years · Gach gnè · Air ùrachadh 28 Sult 2026 · NCT02890342

AAVrh10-PCCA Gene Therapy for Propionic Acidemia

A’ fastadhÌre 1
6 Months – 2 Years · Gach gnè · Air ùrachadh 21 Lùna 2026 · NCT07643844

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

A’ fastadhÌre 1/2
Aoisean 1 agus nas sine · Gach gnè · Air ùrachadh 23 Màrt 2026 · NCT05130437

A Retrospective Study to Characterize Participants With Propionic Acidemia

A’ fastadhSgrùdadh amharc
Aoisean 2 agus nas sine · Gach gnè · Air ùrachadh 5 Gearr 2026 · NCT05769621

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

A’ fastadhÌre 1/2
Gach aois · Gach gnè · Air ùrachadh 22 Faoi 2026 · NCT04159103

An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 15 Gibl 2025 · NCT05040178

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.