Dachaigh › Atrophy Fèitheach an Droma › Arkansas
Sgrùdaidhean clionaigeach Atrophy Fèitheach an Droma ann an Arkansas
Tha 4 sgrùdaidhean airson Atrophy Fèitheach an Droma a’ lorg phàirtichean aig làraichean ann an Arkansas.
Bailtean ann an Arkansas
Teacsa sgrùdaidh oifigeil (Beurla)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- University of Arkansas for Medical Sciences, Little Rock
A’ fastadhÌre 4
3 Months – 24 Months · Gach gnè · Air ùrachadh 2 Dàmh 2026 · NCT05861986A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Arkansas Children's Hospital, Little Rock
A’ fastadhÌre 2
Aoisean 5 gu 17 · Gach gnè · Air ùrachadh 14 Sult 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- University of Arkansas for Medical Sciences, Little Rock
A’ fastadhÌre 4
3 Months – 24 Months · Gach gnè · Air ùrachadh 10 Sult 2026 · NCT05861999Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Arkansas Children's Hospital, Little Rock
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 31 Faoi 2025 · NCT04174157Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.