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Sgrùdaidhean clionaigeach Atrophy Fèitheach an Droma ann an Arkansas

Tha 4 sgrùdaidhean airson Atrophy Fèitheach an Droma a’ lorg phàirtichean aig làraichean ann an Arkansas.

Bailtean ann an Arkansas

Teacsa sgrùdaidh oifigeil (Beurla)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • University of Arkansas for Medical Sciences, Little Rock
A’ fastadhÌre 4
3 Months – 24 Months · Gach gnè · Air ùrachadh 2 Dàmh 2026 · NCT05861986

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • University of Arkansas for Medical Sciences, Little Rock
A’ fastadhÌre 4
3 Months – 24 Months · Gach gnè · Air ùrachadh 10 Sult 2026 · NCT05861999

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Arkansas Children's Hospital, Little Rock
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 31 Faoi 2025 · NCT04174157

Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.