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Sgrùdaidhean clionaigeach Atrophy Fèitheach an Droma ann an Massachusetts
Tha 6 sgrùdaidhean airson Atrophy Fèitheach an Droma a’ lorg phàirtichean aig làraichean ann an Massachusetts.
Bailtean ann an Massachusetts
Teacsa sgrùdaidh oifigeil (Beurla)
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Boston Children's Hospital, Boston
A’ fastadhÌre 2
Aoisean 5 gu 17 · Gach gnè · Air ùrachadh 14 Sult 2026 · NCT07287982A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Boston Children's Hospital, Boston
A’ fastadhÌre 1
Aoisean 3 agus nas sine · Gach gnè · Air ùrachadh 3 Sult 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Boston Children's Hospital, Boston
A’ fastadh
Aoisean 3 agus nas sine · Gach gnè · Air ùrachadh 19 Lùna 2026 · NCT05866419ALS/MND Natural History Study Data Repository
- Lahey Clinic, Burlington
A’ fastadhSgrùdadh amharc
Aoisean 18 gu 90 · Gach gnè · Air ùrachadh 20 Cèit 2026 · NCT05966038Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Boston Children's Hospital, Boston
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 5 agus nas sine · Gach gnè · Air ùrachadh 9 Gibl 2026 · NCT06839469A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Boston Children's Hospital, Boston
A’ fastadhSgrùdadh amharc
Aoisean 18 gu 54 · Banairean · Air ùrachadh 9 Màrt 2026 · NCT05789758Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.