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Sgrùdaidhean clionaigeach Atrophy Fèitheach an Droma ann an Massachusetts

Tha 6 sgrùdaidhean airson Atrophy Fèitheach an Droma a’ lorg phàirtichean aig làraichean ann an Massachusetts.

Bailtean ann an Massachusetts

Teacsa sgrùdaidh oifigeil (Beurla)

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Boston Children's Hospital, Boston
A’ fastadhÌre 1
Aoisean 3 agus nas sine · Gach gnè · Air ùrachadh 3 Sult 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Boston Children's Hospital, Boston
A’ fastadh
Aoisean 3 agus nas sine · Gach gnè · Air ùrachadh 19 Lùna 2026 · NCT05866419

ALS/MND Natural History Study Data Repository

  • Lahey Clinic, Burlington
A’ fastadhSgrùdadh amharc
Aoisean 18 gu 90 · Gach gnè · Air ùrachadh 20 Cèit 2026 · NCT05966038

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Boston Children's Hospital, Boston
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 5 agus nas sine · Gach gnè · Air ùrachadh 9 Gibl 2026 · NCT06839469

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

  • Boston Children's Hospital, Boston
A’ fastadhSgrùdadh amharc
Aoisean 18 gu 54 · Banairean · Air ùrachadh 9 Màrt 2026 · NCT05789758

Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.