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Teacsa sgrùdaidh oifigeil (Beurla)
Recruitment and Apheresis Collection of Peripheral Blood Hematopoietic Stem Cells, Mononuclear Cells and Granulocytes
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 18 gu 70 · Gach gnè · Air ùrachadh 22 Sult 2026 · NCT00001405Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)
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7 Months – 15 Months · Gach gnè · Air ùrachadh 31 Lùna 2026 · NCT06805695Rett Syndrome Registry
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Aoisean 0 gu 99 · Gach gnè · Air ùrachadh 30 Ògmh 2026 · NCT05432349Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
A’ fastadhÌre 3
Aoisean 4 gu 18 · Fir · Air ùrachadh 27 Cèit 2026 · NCT07608432To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome
A’ fastadhÌre 3
Aoisean 5 gu 20 · Banairean · Air ùrachadh 27 Màrt 2026 · NCT06840496Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.