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Rett Syndrome clinical trials in Pennsylvania
5 studies for Rett Syndrome are looking for participants at sites in Pennsylvania.
Cities in Pennsylvania
A Phase 3 Study of Fenfluramine Hydrochloride in Rett Syndrome
- Ep0247 21003, Philadelphia
RecruitingPhase 3
Ages 5 to 35 · All sexes · Updated Oct 2, 2026 · NCT07503444Rett Syndrome Registry
- Children's Hospital of Philadelphia, Philadelphia
RecruitingObservational study
Ages 0 to 99 · All sexes · Updated Jun 30, 2026 · NCT05432349To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome
- Biomed Testing Facility #BIO-17-19104, Philadelphia
RecruitingPhase 3
Ages 5 to 20 · Women · Updated Mar 27, 2026 · NCT06840496ATTUNE: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION440 in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome (MDS)
- Children's Hospital of Philadelphia, Philadelphia
RecruitingPhase 1/2
Ages 2 to 65 · Men · Updated Mar 24, 2026 · NCT06430385Neurophysiologic Biomarkers in Rett Syndrome
- Children's Hospital of Philadelphia, Philadelphia
RecruitingObservational studyHealthy volunteers welcome
Ages 1 to 18 · Women · Updated Oct 20, 2025 · NCT05932589From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.