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Kliničke studije za Gaucherova bolest u državi Pennsylvania

5 studija za Gaucherova bolest traži sudionike na lokacijama u državi Pennsylvania.

Gradovi u državi Pennsylvania

Službeni tekst studije (engleski)

A Gaucher Disease Gene Therapy Trial With FLT201

  • Children's Hospital of Philadelphia, Philadelphia
  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
U tijeku regrutacijaFaza 3
Od 18 godina i više · Oba spola · Ažurirano 3. ruj 2026. · NCT07223944

International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

  • Penn State Health Milton South Hershey Medical Center- Site Number : 840126, Hershey
  • Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
  • Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
  • i još 1
U tijeku regrutacijaOpažajna studija
Sve dobne skupine · Oba spola · Ažurirano 14. tra 2026. · NCT00358943

Longitudinal Study of Neurodegenerative Disorders

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
U tijeku regrutacijaOpažajna studija
Sve dobne skupine · Oba spola · Ažurirano 9. velj 2026. · NCT03333200

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
U tijeku regrutacijaOpažajna studija
2 Months – 60 Years · Oba spola · Ažurirano 13. sij 2026. · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
U tijeku regrutacijaFaza 2
2 Months – 55 Years · Oba spola · Ažurirano 15. pro 2025. · NCT01962415

Iz ClinicalTrials.gov, podaci preuzeti 5. lis 2026.. Svaka studija ima svoje uvjete prihoda; tim studije odlučuje tko se može priključiti.