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Kliničke studije za Genetski poremećaji u državi North Carolina

9 studija za Genetski poremećaji traži sudionike na lokacijama u državi North Carolina.

Gradovi u državi North Carolina

Službeni tekst studije (engleski)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • Duke University Health System, Durham
U tijeku regrutacijaOpažajna studijaZdravi dobrovoljci dobrodošli
1 Month – 100 Years · Oba spola · Ažurirano 2. lis 2026. · NCT02450851

Inherited Reproductive Disorders

  • NIEHS Clinical Research Unit (CRU), Research Triangle Park
U tijeku regrutacijaOpažajna studija
6 Weeks – 120 Years · Oba spola · Ažurirano 28. srp 2026. · NCT01500447

Rett Syndrome Registry

  • The University of North Carolina at Chapel Hill, Chapel Hill
U tijeku regrutacijaOpažajna studija
Od 0 do 99 godina · Oba spola · Ažurirano 30. lip 2026. · NCT05432349

Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)

  • Rare Disease Research, LLC, Hillsborough
U tijeku regrutacijaFaza 3
Od 4 do 18 godina · Muškarci · Ažurirano 27. svi 2026. · NCT07608432

Helix Research Network

  • Cone Health (Gene Connect), Burlington
  • WakeMed (PreciselyYou), Raleigh
U tijeku regrutacijaOpažajna studijaZdravi dobrovoljci dobrodošli
Od 18 godina i više · Oba spola · Ažurirano 23. ožu 2026. · NCT06057181

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • Duke University Medical System (Duke Health), Durham
U tijeku regrutacijaFaza 1/2
Od 1 godina i više · Oba spola · Ažurirano 23. ožu 2026. · NCT05130437

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

  • Levine Children's Hospital - Hematology, Charlotte
U tijeku regrutacijaFaza 3
Od 12 do 35 godina · Oba spola · Ažurirano 23. ožu 2026. · NCT05477563

PKP2-ACM Natural History Study

  • Duke University, Durham
U tijeku regrutacijaOpažajna studija
Od 12 godina i više · Oba spola · Ažurirano 27. velj 2026. · NCT06644742

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Duke University Medical System (Duke Health), Durham
U tijeku regrutacijaFaza 1/2
Sve dobne skupine · Oba spola · Ažurirano 22. sij 2026. · NCT04159103

Iz ClinicalTrials.gov, podaci preuzeti 5. lis 2026.. Svaka studija ima svoje uvjete prihoda; tim studije odlučuje tko se može priključiti.