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Kliničke studije za Urođene greške metabolizma u državi Kalifornija
5 studija za Urođene greške metabolizma traži sudionike na lokacijama u državi Kalifornija.
Gradovi u državi Kalifornija
Službeni tekst studije (engleski)
A Long-Term Observational Study of Patients With Fucosidosis
- Children's Hospital of Orange County, Orange
U tijeku regrutacijaOpažajna studija
Sve dobne skupine · Oba spola · Ažurirano 17. ruj 2026. · NCT07615400Registry of Patients Diagnosed With Lysosomal Storage Diseases
- University of California San Francisco, San Francisco
U tijeku regrutacijaOpažajna studija
Do 64 godina · Oba spola · Ažurirano 8. tra 2026. · NCT05619900A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
- Ronald Reagan UCLA Medical Center, Los Angeles
- University of Stanford Medical Center, Palo Alto
U tijeku regrutacijaFaza 1/2
Od 1 godina i više · Oba spola · Ažurirano 23. ožu 2026. · NCT05130437Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- UCSD Altman Clinical and Transalational Research Institute Building, Los Angeles
- Ronald Reagan UCLA Medical Center, Los Angeles
- Lucile Packard Children's Hospital Stanford, Stanford
U tijeku regrutacijaFaza 1/2
Sve dobne skupine · Oba spola · Ažurirano 22. sij 2026. · NCT04159103An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705
- UCLA Medical Center, Los Angeles
- Lucile Packard Children's Hospital at Stanford, Palo Alto
- Altman Clinical and Translational Research Institution, San Diego
U tijeku regrutacijaFaza 1/2
Od 1 godina i više · Oba spola · Ažurirano 23. pro 2025. · NCT05295433Iz ClinicalTrials.gov, podaci preuzeti 5. lis 2026.. Svaka studija ima svoje uvjete prihoda; tim studije odlučuje tko se može priključiti.