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Kliničke studije za Fenilketonurija u državi Pennsylvania

8 studija za Fenilketonurija traži sudionike na lokacijama u državi Pennsylvania.

Gradovi u državi Pennsylvania

Službeni tekst studije (engleski)

A Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AG-181 in Subjects With Phenylketonuria

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
U tijeku regrutacijaFaza 1
Od 18 do 69 godina · Oba spola · Ažurirano 28. ruj 2026. · NCT07241234

A Study of MZE782 in Adults With PKU

  • Clinic for Special Children, Gordonville
U tijeku regrutacijaFaza 2
Od 18 do 75 godina · Oba spola · Ažurirano 20. kol 2026. · NCT07694440

AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)

  • University of Pittsburgh Medical Center, Pittsburgh
U tijeku regrutacijaFaza 1/2
Od 18 do 55 godina · Oba spola · Ažurirano 18. kol 2026. · NCT06332807

A Study of JNT-517 in Participants With Phenylketonuria (PKU)

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Pittsburgh
U tijeku regrutacijaFaza 3
Od 18 godina i više · Oba spola · Ažurirano 8. srp 2026. · NCT06971731

Immune Modulation During Palynziq® Treatment in Adults (IMPALA)

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Philadelphia
U tijeku regrutacijaFaza 4
Od 18 do 65 godina · Oba spola · Ažurirano 17. lip 2026. · NCT07477691

A Long-Term Study of JNT-517 in Participants With Phenylketonuria

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Pittsburgh
U tijeku regrutacijaFaza 3
Od 4 godina i više · Oba spola · Ažurirano 1. svi 2026. · NCT06628128

A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)

  • University of Pittsburgh Medical Center, Pittsburgh
U tijeku regrutacijaOpažajna studija
Sve dobne skupine · Oba spola · Ažurirano 25. ožu 2026. · NCT05813678

A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)

  • University of Pittsburgh Medical Center, Pittsburgh
U tijeku regrutacijaOpažajna studija
Sve dobne skupine · Oba spola · Ažurirano 24. ožu 2026. · NCT06305234

Iz ClinicalTrials.gov, podaci preuzeti 5. lis 2026.. Svaka studija ima svoje uvjete prihoda; tim studije odlučuje tko se može priključiti.