Početna › Rijetke bolesti › Massachusetts
Kliničke studije za Rijetke bolesti u državi Massachusetts
11 studija za Rijetke bolesti traži sudionike na lokacijama u državi Massachusetts.
Gradovi u državi Massachusetts
Službeni tekst studije (engleski)
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- Massachusetts General Hospital, Boston
- Boston Children s Hospital, Boston
- Brigham and Women's Hospital, Boston
- i još 1
U tijeku regrutacijaOpažajna studijaZdravi dobrovoljci dobrodošli
1 Month – 100 Years · Oba spola · Ažurirano 2. lis 2026. · NCT02450851RAPA-501 Therapy for ALS
- Massachusetts General Hospital, Boston
U tijeku regrutacijaFaza 2/3
Od 18 godina i više · Oba spola · Ažurirano 29. ruj 2026. · NCT04220190A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy
- Boston Children's Hospital, Boston
- University of Massachusetts Chan Medical School, Worcester
U tijeku regrutacijaOpažajna studija
Od 6 godina i više · Oba spola · Ažurirano 2. srp 2026. · NCT07127978Direct to Patient Minimal Risk Biospecimen and Data Collection Research
- Joined Bio, Lexington
U tijeku regrutacijaOpažajna studijaZdravi dobrovoljci dobrodošli
Od 18 do 90 godina · Oba spola · Ažurirano 5. svi 2026. · NCT07128966A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease
- Beth Israel Deaconess Medical Center, Boston
U tijeku regrutacijaFaza 1/2
Od 25 do 65 godina · Oba spola · Ažurirano 5. svi 2026. · NCT06826612A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)
- Massachusetts General Hospital (MGH); Center for Rare Neurological Diseases (CRND), Boston
U tijeku regrutacijaFaza 1/2
30 Months · Oba spola · Ažurirano 17. tra 2026. · NCT04998396Gene Discovery Core, The Manton Center
- Boston Children's Hospital, Boston
U tijeku regrutacijaOpažajna studija
Sve dobne skupine · Oba spola · Ažurirano 25. ožu 2026. · NCT02743845Delineating the Molecular Spectrum and the Clinical, Imaging and Neuronal Phenotype of Chopra-Amiel-Gordon Syndrome
- Boston Children's Hospital, Boston
U tijeku regrutacijaOpažajna studija
Sve dobne skupine · Oba spola · Ažurirano 17. velj 2026. · NCT05528744The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis
- Massachusetts General Hospital, Boston
U tijeku regrutacijaFaza 2
Od 12 godina i više · Oba spola · Ažurirano 1. srp 2025. · NCT04372615A Multi-Site Leukopak Repository Providing Annotated Biospecimens for Approved Investigator-Directed Biomedical Research Initiatives
- Sanguine Biosciences, Waltham
U tijeku regrutacijaOpažajna studijaZdravi dobrovoljci dobrodošli
Od 18 do 89 godina · Oba spola · Ažurirano 6. pro 2024. · NCT05794217Epilepsy Learning Healthcare System (ELHS)
- Partners - Massachusetts General Hospital Epilepsy Service (MGH)/ Partners - Brigham and Women's (BWH), Boston
- Brigham & Women's Hospital, Boston
U tijeku regrutacijaOpažajna studija
Sve dobne skupine · Oba spola · Ažurirano 30. kol 2024. · NCT06265103Iz ClinicalTrials.gov, podaci preuzeti 5. lis 2026.. Svaka studija ima svoje uvjete prihoda; tim studije odlučuje tko se može priključiti.