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Kliničke studije za Spinalna mišićna atrofija u državi Georgia

3 studija za Spinalna mišićna atrofija traži sudionike na lokacijama u državi Georgia.

Gradovi u državi Georgia

Službeni tekst studije (engleski)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta
U tijeku regrutacijaFaza 4
3 Months – 24 Months · Oba spola · Ažurirano 2. lis 2026. · NCT05861986

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • Children's Healthcare of Atlanta, Atlanta
U tijeku regrutacijaFaza 2
Do 2 godina · Oba spola · Ažurirano 2. lis 2026. · NCT07047144

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta
U tijeku regrutacijaFaza 4
3 Months – 24 Months · Oba spola · Ažurirano 10. ruj 2026. · NCT05861999

Iz ClinicalTrials.gov, podaci preuzeti 5. lis 2026.. Svaka studija ima svoje uvjete prihoda; tim studije odlučuje tko se može priključiti.