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Akèy › Adrènoleukodistrofi › Pennsylvania

Etid klinik pou Adrènoleukodistrofi nan Pennsylvania

4 etid pou Adrènoleukodistrofi ap chèche patisipan nan sit nan Pennsylvania.

Vil nan Pennsylvania

Tèks ofisyèl etid la (Anglè)

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Ap rekriteEtid obsèvasyon
2 Months – 60 Years · Tout sèks · Mizajou Jan 13, 2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Ap rekriteFaz 2
2 Months – 55 Years · Tout sèks · Mizajou Dec 15, 2025 · NCT01962415

The Myelin Disorders Biorepository Project

  • The Children's Hospital of Philadelphia, Philadelphia
  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh Medical Center, Pittsburgh
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Oct 23, 2025 · NCT03047369

A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcel

  • Children's Hospital of Philadelphia, Philadelphia
Ap rekriteEtid obsèvasyon
Tout laj · Gason · Mizajou Jul 2, 2025 · NCT06224413

Sous ClinicalTrials.gov, done yo ranmase Oct 1, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.