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5 etid pou Manosidoz Alfa ap rekrite patisipan nan sit atravè Etazini.

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Tèks ofisyèl etid la (Anglè)

UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

Ap rekriteFaz 1
1 Week – 22 Years · Tout sèks · Mizajou Sep 3, 2026 · NCT02254863

Longitudinal Study of Neurodegenerative Disorders

Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Feb 9, 2026 · NCT03333200

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

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2 Months – 60 Years · Tout sèks · Mizajou Jan 13, 2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

Ap rekriteFaz 2
2 Months – 55 Years · Tout sèks · Mizajou Dec 15, 2025 · NCT01962415

Analysis of Velmanase Alfa (Lamzede®)'s Effects in the Body of Children With Alpha-Mannosidosis Under the Age 3

Ap rekriteEtid obsèvasyon
Jiska laj 3 · Tout sèks · Mizajou May 16, 2025 · NCT06184503

Sous ClinicalTrials.gov, done yo ranmase Oct 1, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.