Akèy › Sindrom Angelman › Kalifòni
Etid klinik pou Sindrom Angelman nan Kalifòni
3 etid pou Sindrom Angelman ap chèche patisipan nan sit nan Kalifòni.
Tèks ofisyèl etid la (Anglè)
BEACON - Phase III Clinical Study of Rugonersen in Angelman Syndrome.
- Rady Children's Hospital, San Diego
Ap rekriteFaz 3
Laj 1 a 50 · Tout sèks · Mizajou Sep 10, 2026 · NCT07605429A Phase 1/2 Study of the Safety and Efficacy of MVX-220 in Angelman Syndrome
- Cedars-Sinai Medical Center, Los Angeles
Ap rekriteFaz 1/2
Laj 4 a 50 · Tout sèks · Mizajou Jul 24, 2026 · NCT07181837Angelman Syndrome Natural History Study
- Cedars-Sinai Guerin Children's, Los Angeles
- Rady Children's Hospital, San Diego, San Diego
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Apr 3, 2025 · NCT04507997Sous ClinicalTrials.gov, done yo ranmase Oct 6, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.