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A Phase 1 AAV Gene Therapy Trial Evaluating Safety and Preliminary Efficacy of RP-A701 in Subjects With BAG3 Dilated Cardiomyopathy

  • University of California, San Diego, San Diego
Ap rekriteFaz 1
Laj 18 a 65 · Tout sèks · Mizajou Oct 1, 2026 · NCT07137338

TRITON-CM: A Study to Evaluate Nucresiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy

  • Clinical Trial Site, La Jolla
  • Clinical Trial Site, Laguna Hills
  • Clinical Trial Site, Stanford
Ap rekriteFaz 3
Laj 18 a 85 · Tout sèks · Mizajou Sep 16, 2026 · NCT07052903

DemonsTTRate: A Global, Observational, Multicenter, Long-term Study of Patients With ATTR-CM in a Real-World Setting

  • Clinical Trial Site, Beverly Hills
Ap rekriteEtid obsèvasyon
Laj 18 ak plis · Tout sèks · Mizajou Sep 9, 2026 · NCT07358078

Clinical Course Of Disease In Participants With FA-CM

  • University of California San Diego, La Jolla
Ap rekriteEtid obsèvasyon
Laj 6 ak plis · Tout sèks · Mizajou Sep 2, 2026 · NCT06865482

Multicenter Trial of ECMO in Children With Severe Cardiac Failure Using the Cardiohelp System

  • Lucile Packard Children's Hospital, Palo Alto
Ap rekriteFaz 2
Laj 0 a 16 · Tout sèks · Mizajou Aug 10, 2026 · NCT06080074

Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant

  • University of California, San Diego (UCSD) - Medical Center, La Jolla
  • University of California, Los Angeles (UCLA) - David Geffen School of Medicine, Los Angeles
  • University of California, San Francisco (UCSF), San Francisco
  • ak 1 plis
Ap rekriteFaz 3
Laj 18 a 75 · Tout sèks · Mizajou Aug 4, 2026 · NCT06563895

Danon Disease Natural History Study

  • University of California, San Diego, La Jolla
Ap rekriteEtid obsèvasyon
Laj 8 ak plis · Tout sèks · Mizajou Jul 28, 2026 · NCT06214507

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

  • UC Davis, Sacramento
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jul 28, 2026 · NCT07674758

The PIVATAL Study -Study of Ventricular Arrhythmia (VTA) Ablation in Left Ventricular Assist Device (LVAD) Patients

  • UCLA Cardiac Arrthmia Center, Los Angeles
  • University of California San Francisco, San Francisco
Ap rekriteFaz 4
Laj 18 ak plis · Tout sèks · Mizajou Jul 14, 2026 · NCT05034432

A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease

  • University of California, San Diego, La Jolla
Ap rekriteFaz 2
Laj 8 ak plis · Gason · Mizajou May 4, 2026 · NCT06092034

MAGNITUDE: A Phase 3 Study of NTLA-2001 in Participants With Transthyretin Amyloidosis With Cardiomyopathy (ATTR-CM)

  • Cedars-Sinai Medical Center, Los Angeles
  • Western Greater Los Angeles VA Medical Center, Los Angeles
  • Stanford University, Palo Alto
  • ak 1 plis
Ap rekriteFaz 3
Laj 18 a 90 · Tout sèks · Mizajou Mar 27, 2026 · NCT06128629

A Study to Assess Real-world Patient Characteristics and Clinical Course for Symptomatic Patients With PKP2-ACM

  • Leland Stanford Junior University, Redwood City
Ap rekriteEtid obsèvasyon
Laj 18 a 65 · Tout sèks · Mizajou May 16, 2025 · NCT06976606

Large Language Models To Improve the Quality of Care of Cardiology Patients

  • Stanford, Palo Alto
Ap rekrite
Laj 18 ak plis · Tout sèks · Mizajou May 15, 2025 · NCT06935253

Mesenchymal Stem Cells for the Treatment of Various Chronic and Acute Conditions

  • Southern California Hospital at Culver City / Southern California Hospital at Hollywood / Multiple US-based Sub-Investigator Sites, Culver City
Ap rekriteFaz 1/2Volontè an sante akeyi
Laj 18 ak plis · Tout sèks · Mizajou Apr 29, 2022 · NCT04684602

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.