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A Phase 1 AAV Gene Therapy Trial Evaluating Safety and Preliminary Efficacy of RP-A701 in Subjects With BAG3 Dilated Cardiomyopathy
- University of California, San Diego, San Diego
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Laj 18 a 65 · Tout sèks · Mizajou Oct 1, 2026 · NCT07137338TRITON-CM: A Study to Evaluate Nucresiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy
- Clinical Trial Site, La Jolla
- Clinical Trial Site, Laguna Hills
- Clinical Trial Site, Stanford
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Laj 18 a 85 · Tout sèks · Mizajou Sep 16, 2026 · NCT07052903DemonsTTRate: A Global, Observational, Multicenter, Long-term Study of Patients With ATTR-CM in a Real-World Setting
- Clinical Trial Site, Beverly Hills
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Laj 18 ak plis · Tout sèks · Mizajou Sep 9, 2026 · NCT07358078Clinical Course Of Disease In Participants With FA-CM
- University of California San Diego, La Jolla
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Laj 6 ak plis · Tout sèks · Mizajou Sep 2, 2026 · NCT06865482Multicenter Trial of ECMO in Children With Severe Cardiac Failure Using the Cardiohelp System
- Lucile Packard Children's Hospital, Palo Alto
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Laj 0 a 16 · Tout sèks · Mizajou Aug 10, 2026 · NCT06080074Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant
- University of California, San Diego (UCSD) - Medical Center, La Jolla
- University of California, Los Angeles (UCLA) - David Geffen School of Medicine, Los Angeles
- University of California, San Francisco (UCSF), San Francisco
- ak 1 plis
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Laj 18 a 75 · Tout sèks · Mizajou Aug 4, 2026 · NCT06563895Danon Disease Natural History Study
- University of California, San Diego, La Jolla
Ap rekriteEtid obsèvasyon
Laj 8 ak plis · Tout sèks · Mizajou Jul 28, 2026 · NCT06214507Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials
- UC Davis, Sacramento
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Tout laj · Tout sèks · Mizajou Jul 28, 2026 · NCT07674758The PIVATAL Study -Study of Ventricular Arrhythmia (VTA) Ablation in Left Ventricular Assist Device (LVAD) Patients
- UCLA Cardiac Arrthmia Center, Los Angeles
- University of California San Francisco, San Francisco
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Laj 18 ak plis · Tout sèks · Mizajou Jul 14, 2026 · NCT05034432A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease
- University of California, San Diego, La Jolla
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Laj 8 ak plis · Gason · Mizajou May 4, 2026 · NCT06092034MAGNITUDE: A Phase 3 Study of NTLA-2001 in Participants With Transthyretin Amyloidosis With Cardiomyopathy (ATTR-CM)
- Cedars-Sinai Medical Center, Los Angeles
- Western Greater Los Angeles VA Medical Center, Los Angeles
- Stanford University, Palo Alto
- ak 1 plis
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Laj 18 a 90 · Tout sèks · Mizajou Mar 27, 2026 · NCT06128629A Study to Assess Real-world Patient Characteristics and Clinical Course for Symptomatic Patients With PKP2-ACM
- Leland Stanford Junior University, Redwood City
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Laj 18 a 65 · Tout sèks · Mizajou May 16, 2025 · NCT06976606Large Language Models To Improve the Quality of Care of Cardiology Patients
- Stanford, Palo Alto
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Laj 18 ak plis · Tout sèks · Mizajou May 15, 2025 · NCT06935253Mesenchymal Stem Cells for the Treatment of Various Chronic and Acute Conditions
- Southern California Hospital at Culver City / Southern California Hospital at Hollywood / Multiple US-based Sub-Investigator Sites, Culver City
Ap rekriteFaz 1/2Volontè an sante akeyi
Laj 18 ak plis · Tout sèks · Mizajou Apr 29, 2022 · NCT04684602Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.