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Akèy › Maladi Fabry › Pennsylvania

Etid klinik pou Maladi Fabry nan Pennsylvania

5 etid pou Maladi Fabry ap chèche patisipan nan sit nan Pennsylvania.

Vil nan Pennsylvania

Tèks ofisyèl etid la (Anglè)

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Ap rekriteFaz 1/2
Laj 18 a 65 · Gason · Mizajou Sep 24, 2026 · NCT06270316

A Study of Patients With Fabry Disease (US Specific)

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Ap rekriteEtid obsèvasyon
Laj 18 ak plis · Tout sèks · Mizajou Sep 9, 2026 · NCT06906367

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Ap rekriteFaz 3
Laj 2 a 11 · Tout sèks · Mizajou Sep 1, 2026 · NCT06904261

Fabry Disease Registry & Pregnancy Sub-registry

  • Geisinger Medical Center- Site Number : 840111, Danville
  • Penn State University Medical Center-Neurology- Site Number : 840104, Hershey
  • Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
  • ak 2 plis
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jun 23, 2026 · NCT00196742

A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding

  • Amicus Therapeutics, Inc. Pregnancy Registry, Philadelphia
Ap rekriteEtid obsèvasyon
Tout laj · Fanm · Mizajou Jul 8, 2025 · NCT04252066

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.