Akèy › Maladi Fabry › Pennsylvania
Etid klinik pou Maladi Fabry nan Pennsylvania
5 etid pou Maladi Fabry ap chèche patisipan nan sit nan Pennsylvania.
Vil nan Pennsylvania
Tèks ofisyèl etid la (Anglè)
Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Ap rekriteFaz 1/2
Laj 18 a 65 · Gason · Mizajou Sep 24, 2026 · NCT06270316A Study of Patients With Fabry Disease (US Specific)
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Ap rekriteEtid obsèvasyon
Laj 18 ak plis · Tout sèks · Mizajou Sep 9, 2026 · NCT06906367A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Ap rekriteFaz 3
Laj 2 a 11 · Tout sèks · Mizajou Sep 1, 2026 · NCT06904261Fabry Disease Registry & Pregnancy Sub-registry
- Geisinger Medical Center- Site Number : 840111, Danville
- Penn State University Medical Center-Neurology- Site Number : 840104, Hershey
- Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
- ak 2 plis
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jun 23, 2026 · NCT00196742A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding
- Amicus Therapeutics, Inc. Pregnancy Registry, Philadelphia
Ap rekriteEtid obsèvasyon
Tout laj · Fanm · Mizajou Jul 8, 2025 · NCT04252066Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.