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Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively

  • The Regents of the University of California||UC Davis Health, Rancho Cordova
  • UC Davis Health, Sacramento
  • UC Davis Ambulatory Care Clinic, Sacramento
  • ak 3 plis
Ap rekriteFaz 3
Laj 18 ak plis · Gason · Mizajou Oct 2, 2026 · NCT05568719

A Study to Test a Medicine (Fitusiran) for Preventing Bleeds in People With Severe Hemophilia Who Previously Received Preventive Treatment With Emicizumab

  • Children's Hospital Los Angeles- Site Number : 8400005, Los Angeles
Ap rekriteFaz 4
Laj 12 ak plis · Gason · Mizajou Sep 23, 2026 · NCT06145373

A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of NXT007 in Persons With Severe or Moderate Hemophilia A

  • UC Davis Cancer Center, Sacramento
Ap rekriteFaz 1/2
Laj 2 a 59 · Gason · Mizajou Sep 11, 2026 · NCT05987449

A Gene Therapy Study of SPK-8011QQ in Adults With Severe or Moderately Severe Hemophilia A

  • Center for Inherited Blood Disorders, Orange
  • University of California San Francisco, San Francisco
  • Kaiser Permanente, Vallejo
Ap rekriteFaz 1/2
Laj 18 ak plis · Gason · Mizajou Sep 11, 2026 · NCT07226206

A Clinical Study to Evaluate the Effects of NXT007 Compared to Emicizumab Prophylaxis in People With Hemophilia A

  • Center for Inherited Blood Disorders, Orange
Ap rekriteFaz 3
Laj 12 ak plis · Tout sèks · Mizajou Sep 4, 2026 · NCT07416604

Pharmacokinetics, Pharmacodynamics, and Safety Profile of Understudied Drugs Administered to Children Per Standard of Care (POPS)

  • Lucile Packard Children's Hospital, Palo Alto
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 0 a 20 · Tout sèks · Mizajou Aug 21, 2026 · NCT04278404

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Orthopaedic Institute for Children HTC, Los Angeles
  • Childrens Hospital Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital Oakland, Oakland
  • ak 5 plis
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Aug 17, 2026 · NCT04398628

A Study to Investigate the Efficacy and Safety of Fitusiran Prophylaxis in Male Participants Aged 1 to Less Than 12 Years With Hemophilia A or B

  • The Luskin Orthopaedic Institute for Children- Site Number : 8400013, Los Angeles
  • The Center for Inherited Blood Disorders- Site Number : 8400009, Orange
Ap rekriteFaz 3
Laj 1 a 11 · Gason · Mizajou Aug 17, 2026 · NCT07285460

Prevention of Bleeding in Patients With Moderate and Severe Hemophilia A Playing Sports: A Comparison Between Factor VIII and Emicizumab Prophylaxis

  • Stanford University, Palo Alto
  • Rady Children's Hospital, San Diego
Ap rekriteEtid obsèvasyon
Laj 6 a 19 · Tout sèks · Mizajou Jul 2, 2026 · NCT05022459

A Study to Learn About How Changing Therapy From Emicizumab to Marstacimab Affects People With the Severe Hemophilia A.

  • Orthopaedic Institute for Children/Orthopaedic Hemophilia Treatment Center, Los Angeles
Ap rekriteFaz 1
Laj 12 a 74 · Gason · Mizajou Jun 3, 2026 · NCT06703606

Emicizumab for Severe Von Willebrand Disease (VWD) and VWD/Hemophilia A

  • The Center for Comprehensive Care and Diagnosis of Inherited Blood Disorders (CIBD), Orange
  • Stanford University: Stanford Children's Health, Redwood City
Ap rekriteFaz 1
Laj 0 a 90 · Tout sèks · Mizajou Apr 3, 2026 · NCT05500807

SEVENFACT® for Bleeding Events in Hemophilia With Inhibitors

  • Orthopaedic Institute for Children, Los Angeles
  • University of California at Davis UC Davis Hemostasis and Thrombosis Center, Sacramento
Ap rekriteFaz 4
Laj 12 a 100 · Tout sèks · Mizajou Jan 12, 2026 · NCT04647227

Efanesoctocog Alfa Prophylaxis in Patients With Hemophilia A With Synovial Hypertrophy

  • Orthopedic Institute for Children- Site Number : 8400009, Los Angeles
Ap rekriteFaz 4
Laj 12 ak plis · Tout sèks · Mizajou Nov 18, 2025 · NCT06941870

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.