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Tèks ofisyèl etid la (Anglè)

UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

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1 Week – 22 Years · Tout sèks · Mizajou Sep 3, 2026 · NCT02254863

Krabbe Disease Global Patient Registry

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Tout laj · Tout sèks · Mizajou Jul 17, 2026 · NCT02993796

A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)

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30 Months · Tout sèks · Mizajou Apr 17, 2026 · NCT04998396

Longitudinal Study of Neurodegenerative Disorders

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Tout laj · Tout sèks · Mizajou Feb 9, 2026 · NCT03333200

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

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2 Months – 60 Years · Tout sèks · Mizajou Jan 13, 2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

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2 Months – 55 Years · Tout sèks · Mizajou Dec 15, 2025 · NCT01962415

The Myelin Disorders Biorepository Project

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Tout laj · Tout sèks · Mizajou Oct 23, 2025 · NCT03047369

Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford

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Tout laj · Tout sèks · Mizajou May 29, 2025 · NCT01793168

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.