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Tèks ofisyèl etid la (Anglè)

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

  • UCSD - Altman Clinical and Translational Research Institute, La Jolla
  • UCLA Medical Center (Department of Neurology), Los Angeles
  • Stanford Neuroscience Health Center, Palo Alto
Ap rekriteFaz 3
Laj 16 ak plis · Tout sèks · Mizajou Oct 1, 2026 · NCT07486934

DMCRN-02-001: Assessing Pediatric Endpoints in DM1

  • University of California, Los Angeles, Los Angeles
Ap rekriteEtid obsèvasyon
59 Months · Tout sèks · Mizajou Jun 10, 2026 · NCT05224778

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

  • University of California, San Diego, La Jolla
  • University of California, Los Angeles, Los Angeles
Ap rekriteEtid obsèvasyon
Laj 18 a 70 · Tout sèks · Mizajou Jun 10, 2026 · NCT03981575

Study of ATX-01 in Participants With DM1

  • UCLA, Los Angeles
Ap rekriteFaz 1/2
Laj 18 a 64 · Tout sèks · Mizajou Feb 10, 2026 · NCT06300307

Myotonic Dystrophy Family Registry

  • Myotonic Dystrophy Foundation, Oakland
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Nov 21, 2024 · NCT02398786

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.