Akèy › Distrofi myotonik › Florid
Etid klinik pou Distrofi myotonik nan Florid
3 etid pou Distrofi myotonik ap chèche patisipan nan sit nan Florid.
Vil nan Florid
Tèks ofisyèl etid la (Anglè)
A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
- University of Florida, 2004 Mowry Road - Site Number: 8400005, Gainesville
- University of South Florida - Neuromuscular Research, 13330 USF Laurel Drive - Site Number: 8400001, Tampa
Ap rekriteFaz 1/2
Laj 10 a 55 · Tout sèks · Mizajou Sep 21, 2026 · NCT06844214Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
- University of Florida, Gainesville
Ap rekriteEtid obsèvasyon
Laj 18 a 70 · Tout sèks · Mizajou Jun 10, 2026 · NCT03981575Study of ATX-01 in Participants With DM1
- University of Florida, Gainesville
Ap rekriteFaz 1/2
Laj 18 a 64 · Tout sèks · Mizajou Feb 10, 2026 · NCT06300307Sous ClinicalTrials.gov, done yo ranmase Oct 2, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.