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Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension
- University of Kansas Medical Center, Kansas City
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Laj 3 a 17 · Tout sèks · Mizajou Aug 11, 2026 · NCT06747884Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
- Kansas University Medical Center, Kansas City
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Laj 18 a 70 · Tout sèks · Mizajou Jun 10, 2026 · NCT03981575DMCRN-02-001: Assessing Pediatric Endpoints in DM1
- University of Kansas Medical Center, Fairway
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59 Months · Tout sèks · Mizajou Jun 10, 2026 · NCT05224778Study of ATX-01 in Participants With DM1
- University of Kansas Medical Center, Department of Neurology, Fairway
Ap rekriteFaz 1/2
Laj 18 a 64 · Tout sèks · Mizajou Feb 10, 2026 · NCT06300307Sous ClinicalTrials.gov, done yo ranmase Oct 1, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.