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Etid klinik pou Distrofi myotonik nan New York
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Tèks ofisyèl etid la (Anglè)
Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
- University of Rochester Medical Center, Rochester
Ap rekriteFaz 3
Laj 16 ak plis · Tout sèks · Mizajou Oct 1, 2026 · NCT07486934A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
- Columbia University Medical Center - Neurological Institute, 710 W. 168th, 2nd floor, suite 204 - Site Number : 8400003, New York
Ap rekriteFaz 1/2
Laj 10 a 55 · Tout sèks · Mizajou Sep 21, 2026 · NCT06844214DMCRN-02-001: Assessing Pediatric Endpoints in DM1
- University of Rochester Medical Center, Rochester
Ap rekriteEtid obsèvasyon
59 Months · Tout sèks · Mizajou Jun 10, 2026 · NCT05224778Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
- University of Rochester, Rochester
Ap rekriteEtid obsèvasyon
Laj 18 a 70 · Tout sèks · Mizajou Jun 10, 2026 · NCT03981575Remote Assessments and Genetic Determinants of Congenital and Childhood Myotonic Dystrophy
- University of Rochester, Rochester
Ap rekriteEtid obsèvasyon
Laj 0 a 17 · Tout sèks · Mizajou Jun 5, 2026 · NCT07630389Remote Assessments and Genetic Determinants of Myotonic Dystrophy
- University of Rochester, Rochester
Ap rekriteEtid obsèvasyon
Laj 18 a 88 · Tout sèks · Mizajou Apr 1, 2026 · NCT07505342Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
- University of Rochester Medical Center, Department of Neurology, Rochester
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Tout laj · Tout sèks · Mizajou Oct 15, 2025 · NCT00082108Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy
- University of Rochester - Medical Center, Rochester
Ap rekriteFaz 2/3
Laj 6 a 45 · Tout sèks · Mizajou May 28, 2025 · NCT05004129Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.