Akèy › Distrofi myotonik › North Carolina
Etid klinik pou Distrofi myotonik nan North Carolina
4 etid pou Distrofi myotonik ap chèche patisipan nan sit nan North Carolina.
Tèks ofisyèl etid la (Anglè)
Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
- Rare Disease Research, LLC, Hillsborough
Ap rekriteFaz 3
Laj 16 ak plis · Tout sèks · Mizajou Oct 1, 2026 · NCT07486934Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
- Rare Disease Research, LLC, Hillsborough
Ap rekriteFaz 3
Laj 4 a 18 · Gason · Mizajou May 27, 2026 · NCT07608432Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic Dystrophy
- Wake Forest University Health Sciences, Winston-Salem
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 18 a 65 · Tout sèks · Mizajou Jan 23, 2026 · NCT07362875Biomarker Development for Muscular Dystrophies
- Wake Forest University, Winston-Salem
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 5 ak plis · Tout sèks · Mizajou Nov 24, 2025 · NCT05019625Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.