Akèy › Distrofi myotonik › Pennsylvania
Etid klinik pou Distrofi myotonik nan Pennsylvania
3 etid pou Distrofi myotonik ap chèche patisipan nan sit nan Pennsylvania.
Tèks ofisyèl etid la (Anglè)
A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
- Penn Medicine: University of Pennsylvania Health System- Site Number : 8400009, Philadelphia
Ap rekriteFaz 1/2
Laj 10 a 55 · Tout sèks · Mizajou Sep 21, 2026 · NCT06844214Biomarker Development for Muscular Dystrophies
- University of Pittsburgh, Pittsburgh
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 5 ak plis · Tout sèks · Mizajou Nov 24, 2025 · NCT05019625Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy
- University of Pittsburgh Medical Center, Pittsburgh
Ap rekriteFaz 2/3
Laj 6 a 45 · Tout sèks · Mizajou May 28, 2025 · NCT05004129Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.