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Akèy › Distrofi myotonik › Virginia › Richmond

Etid klinik pou Distrofi myotonik nan Richmond, VA

8 etid pou Distrofi myotonik ap chèche patisipan nan sit nan ak bò kote Richmond (nan yon distans apeprè 30 mil). Louvri yon etid pou wè ki moun ki ka patisipe ak kijan pou kontakte ekip etid la.

Tèks ofisyèl etid la (Anglè)

Ap chèche patisipan pou yon etid? Mete l anwo paj sa a — $99 pou 30 jou →

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

Ap rekriteFaz 3
  • Virginia Commonwealth University - Biotech One, Richmond
Laj 16 ak plis · Tout sèks · Mizajou Oct 1, 2026 · NCT07486934

A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1

Ap rekriteFaz 1/2
  • Virginia Commonwealth University Medical Center- Site Number : 8400006, Richmond
Laj 10 a 55 · Tout sèks · Mizajou Sep 21, 2026 · NCT06844214

Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension

Ap rekriteEtid obsèvasyon
  • Virginia Commonwealth University, Richmond
Laj 18 a 70 · Tout sèks · Mizajou Sep 4, 2026 · NCT07700225

Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

Ap rekriteEtid obsèvasyon
  • Virginia Commonwealth University, Richmond
Laj 3 a 17 · Tout sèks · Mizajou Aug 11, 2026 · NCT06747884

DMCRN-02-001: Assessing Pediatric Endpoints in DM1

Ap rekriteEtid obsèvasyon
  • Virginia Commonwealth University, Richmond
59 Months · Tout sèks · Mizajou Jun 10, 2026 · NCT05224778

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

Ap rekriteEtid obsèvasyon
  • Virginia Commonwealth University, Richmond
Laj 18 a 70 · Tout sèks · Mizajou Jun 10, 2026 · NCT03981575

Study of ATX-01 in Participants With DM1

Ap rekriteFaz 1/2
  • Virginia Commonwealth University, Richmond
Laj 18 a 64 · Tout sèks · Mizajou Feb 10, 2026 · NCT06300307

Long-Term Development of Muscular Dystrophy Outcome Assessments

Ap rekriteEtid obsèvasyon
  • Virginia Commonwealth University, Richmond
Laj 6 a 50 · Tout sèks · Mizajou Nov 18, 2025 · NCT05989620

Etid Distrofi myotonik nan lòt vil

Lòt etid nan Richmond

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.