Akèy › Maladi Pelizaeus-Merzbacher › Pennsylvania
Etid klinik pou Maladi Pelizaeus-Merzbacher nan Pennsylvania
4 etid pou Maladi Pelizaeus-Merzbacher ap chèche patisipan nan sit nan Pennsylvania.
Vil nan Pennsylvania
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Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease
- Ionis Investigative Site, Philadelphia
Ap rekriteEtid obsèvasyon
6 Months – 17 Years · Gason · Mizajou Oct 2, 2026 · NCT05659901Longitudinal Study of Neurodegenerative Disorders
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
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Tout laj · Tout sèks · Mizajou Feb 9, 2026 · NCT03333200Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)
- Ionis Investigative Site, Philadelphia
Ap rekriteFaz 1
Laj 2 a 17 · Gason · Mizajou Dec 12, 2025 · NCT06150716The Myelin Disorders Biorepository Project
- The Children's Hospital of Philadelphia, Philadelphia
- University of Pennsylvania, Philadelphia
- University of Pittsburgh Medical Center, Pittsburgh
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Oct 23, 2025 · NCT03047369Sous ClinicalTrials.gov, done yo ranmase Oct 6, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.