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Akèy › Fenilketonuri › Pennsylvania

Etid klinik pou Fenilketonuri nan Pennsylvania

8 etid pou Fenilketonuri ap chèche patisipan nan sit nan Pennsylvania.

Vil nan Pennsylvania

Tèks ofisyèl etid la (Anglè)

A Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AG-181 in Subjects With Phenylketonuria

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Ap rekriteFaz 1
Laj 18 a 69 · Tout sèks · Mizajou Sep 28, 2026 · NCT07241234

A Study of MZE782 in Adults With PKU

  • Clinic for Special Children, Gordonville
Ap rekriteFaz 2
Laj 18 a 75 · Tout sèks · Mizajou Aug 20, 2026 · NCT07694440

AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)

  • University of Pittsburgh Medical Center, Pittsburgh
Ap rekriteFaz 1/2
Laj 18 a 55 · Tout sèks · Mizajou Aug 18, 2026 · NCT06332807

A Study of JNT-517 in Participants With Phenylketonuria (PKU)

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Pittsburgh
Ap rekriteFaz 3
Laj 18 ak plis · Tout sèks · Mizajou Jul 8, 2026 · NCT06971731

Immune Modulation During Palynziq® Treatment in Adults (IMPALA)

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Philadelphia
Ap rekriteFaz 4
Laj 18 a 65 · Tout sèks · Mizajou Jun 17, 2026 · NCT07477691

A Long-Term Study of JNT-517 in Participants With Phenylketonuria

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Pittsburgh
Ap rekriteFaz 3
Laj 4 ak plis · Tout sèks · Mizajou May 1, 2026 · NCT06628128

A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)

  • University of Pittsburgh Medical Center, Pittsburgh
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Mar 25, 2026 · NCT05813678

A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)

  • University of Pittsburgh Medical Center, Pittsburgh
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Mar 24, 2026 · NCT06305234

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.