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Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
1 Month – 100 Years · Tout sèks · Mizajou Sep 28, 2026 · NCT02890342

AAVrh10-PCCA Gene Therapy for Propionic Acidemia

Ap rekriteFaz 1
6 Months – 2 Years · Tout sèks · Mizajou Aug 21, 2026 · NCT07643844

A Retrospective Study to Characterize Participants With Propionic Acidemia

Ap rekriteEtid obsèvasyon
Laj 2 ak plis · Tout sèks · Mizajou Feb 5, 2026 · NCT05769621

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

Ap rekriteFaz 1/2
Tout laj · Tout sèks · Mizajou Jan 22, 2026 · NCT04159103

An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics

Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Apr 15, 2025 · NCT05040178

Sous ClinicalTrials.gov, done yo ranmase Oct 2, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.