Akèy › Asidemi propiyonik
Etid klinik pou Asidemi propiyonik ap rekrite nan Etazini
6 etid pou Asidemi propiyonik ap rekrite patisipan nan sit atravè Etazini.
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Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
1 Month – 100 Years · Tout sèks · Mizajou Sep 28, 2026 · NCT02890342AAVrh10-PCCA Gene Therapy for Propionic Acidemia
Ap rekriteFaz 1
6 Months – 2 Years · Tout sèks · Mizajou Aug 21, 2026 · NCT07643844A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
Ap rekriteFaz 1/2
Laj 1 ak plis · Tout sèks · Mizajou Mar 23, 2026 · NCT05130437A Retrospective Study to Characterize Participants With Propionic Acidemia
Ap rekriteEtid obsèvasyon
Laj 2 ak plis · Tout sèks · Mizajou Feb 5, 2026 · NCT05769621Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
Ap rekriteFaz 1/2
Tout laj · Tout sèks · Mizajou Jan 22, 2026 · NCT04159103An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics
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Tout laj · Tout sèks · Mizajou Apr 15, 2025 · NCT05040178Sous ClinicalTrials.gov, done yo ranmase Oct 2, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.