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Etid klinik pou Atrofi miskilè spinal nan Arkansas
4 etid pou Atrofi miskilè spinal ap chèche patisipan nan sit nan Arkansas.
Vil nan Arkansas
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A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- University of Arkansas for Medical Sciences, Little Rock
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3 Months – 24 Months · Tout sèks · Mizajou Oct 2, 2026 · NCT05861986A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Arkansas Children's Hospital, Little Rock
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Laj 5 a 17 · Tout sèks · Mizajou Sep 14, 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- University of Arkansas for Medical Sciences, Little Rock
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3 Months – 24 Months · Tout sèks · Mizajou Sep 10, 2026 · NCT05861999Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Arkansas Children's Hospital, Little Rock
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jan 31, 2025 · NCT04174157Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.