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Akèy › Atrofi miskilè spinal › Florid › Gainesville

Etid klinik pou Atrofi miskilè spinal nan Gainesville, FL

3 etid pou Atrofi miskilè spinal ap chèche patisipan nan sit nan ak bò kote Gainesville (nan yon distans apeprè 30 mil). Louvri yon etid pou wè ki moun ki ka patisipe ak kijan pou kontakte ekip etid la.

Tèks ofisyèl etid la (Anglè)

Ap chèche patisipan pou yon etid? Mete l anwo paj sa a — $99 pou 30 jou →

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

Ap rekriteFaz 4
  • University of Florida Pediatrics, Gainesville
3 Months – 24 Months · Tout sèks · Mizajou Oct 2, 2026 · NCT05861986

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

Ap rekriteFaz 4
  • University of Florida Pediatrics, Gainesville
3 Months – 24 Months · Tout sèks · Mizajou Sep 10, 2026 · NCT05861999

ALS/MND Natural History Study Data Repository

Ap rekriteEtid obsèvasyon
  • University of Florida, Gainesville
Laj 18 a 90 · Tout sèks · Mizajou May 20, 2026 · NCT05966038

Etid Atrofi miskilè spinal nan lòt vil

Lòt etid nan Gainesville

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.