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Etid klinik pou Atrofi miskilè spinal nan Missouri

4 etid pou Atrofi miskilè spinal ap chèche patisipan nan sit nan Missouri.

Vil nan Missouri

Tèks ofisyèl etid la (Anglè)

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • The Curators of the University of Missouri on behalf of University of Missouri Health Care, Columbia
Ap rekriteFaz 2
Laj 5 a 17 · Tout sèks · Mizajou Sep 14, 2026 · NCT07287982

ALS/MND Natural History Study Data Repository

  • Saint Louis University, St Louis
Ap rekriteEtid obsèvasyon
Laj 18 a 90 · Tout sèks · Mizajou May 20, 2026 · NCT05966038

Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease

  • NextGen Precision Health Building, Clinical and Translational Science Unit, Columbia
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Laj 18 ak plis · Tout sèks · Mizajou Mar 17, 2026 · NCT07478172

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • University of Missouri Health System, Columbia
  • Washington University School of Medicine in St. Louis, St Louis
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jan 31, 2025 · NCT04174157

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.