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A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Stacey Hall Developmental Pediatrics, Charlottesville
  • Children's Hospital of the King's Daughters_Norfolk, Norfolk
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Laj 3 ak plis · Tout sèks · Mizajou Sep 3, 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • University of Virginia, Charlottesville
  • Childrens Hospital of the King's Daughters, Norfolk
Ap rekrite
Laj 3 ak plis · Tout sèks · Mizajou Aug 19, 2026 · NCT05866419

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

  • Childrens Hospital of the Kings Daughter Norfolk, Norfolk
Ap rekriteFaz 3
0 Days – 42 Days · Tout sèks · Mizajou Aug 18, 2026 · NCT07221669

ALS/MND Natural History Study Data Repository

  • Virginia Commonwealth University, Richmond
Ap rekriteEtid obsèvasyon
Laj 18 a 90 · Tout sèks · Mizajou May 20, 2026 · NCT05966038

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • University of Virginia Health System, Charlottesville
  • Children's Hospital of The King's Daughters, Norfolk
  • Virginia Commonwealth University Health System, Richmond
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jan 31, 2025 · NCT04174157

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.