Akèy › Amiloidoz ereditè ki gen rapò ak transthyretin › Pennsylvania
Etid klinik pou Amiloidoz ereditè ki gen rapò ak transthyretin nan Pennsylvania
4 etid pou Amiloidoz ereditè ki gen rapò ak transthyretin ap chèche patisipan nan sit nan Pennsylvania.
Vil nan Pennsylvania
Tèks ofisyèl etid la (Anglè)
Non-interventional Study of Patients With Transthyretin (ATTR) Amyloidosis
- Research Site, Danville
- Research Site, Philadelphia
- Research Site, Philadelphia
Ap rekriteEtid obsèvasyon
Laj 18 a 130 · Tout sèks · Mizajou Sep 23, 2026 · NCT06465810ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)
- Clinical Trial Site, Philadelphia
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Sep 8, 2026 · NCT04561518Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant
- Penn Presbyterian Medical Center, Philadelphia
- University of Pittsburgh Medical Center, Presbyterian Hospital, Pittsburgh
Ap rekriteFaz 3
Laj 18 a 75 · Tout sèks · Mizajou Aug 4, 2026 · NCT06563895MAGNITUDE: A Phase 3 Study of NTLA-2001 in Participants With Transthyretin Amyloidosis With Cardiomyopathy (ATTR-CM)
- Penn Presbyterian Medical Center, Philadelphia
- Allegheny General Hospital, Pittsburgh
- University of Pittsburgh Medical Center, Pittsburgh
Ap rekriteFaz 3
Laj 18 a 90 · Tout sèks · Mizajou Mar 27, 2026 · NCT06128629Sous ClinicalTrials.gov, done yo ranmase Oct 6, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.